Trials / Completed
CompletedNCT03096782
Umbilical Cord Blood Transplant With Added Sugar and Chemotherapy and Radiation Therapy in Treating Patients With Leukemia or Lymphoma
Cord Blood Ex-Vivo MSC Expansion Plus Fucosylation to Enhance Homing and Engraftment
- Status
- Completed
- Phase
- Phase 2
- Study type
- Interventional
- Enrollment
- 6 (actual)
- Sponsor
- M.D. Anderson Cancer Center · Academic / Other
- Sex
- All
- Age
- 12 Years – 65 Years
- Healthy volunteers
- Not accepted
Summary
This phase II trial studies how well an umbilical cord blood transplant with added sugar works with chemotherapy and radiation therapy in treating patients with leukemia or lymphoma. Giving chemotherapy and total-body irradiation before a donor umbilical cord blood transplant helps stop the growth of cells in the bone marrow, including normal blood-forming cells (stem cells) and cancer cells. When the healthy stem cells from a donor are infused into the patient they may help the patient's bone marrow make stem cells, red blood cells, white blood cells, and platelets. The umbilical cord blood cells will be grown ("expanded") on a special layer of cells collected from the bone marrow of healthy volunteers in a laboratory. A type of sugar will also be added to the cells in the laboratory that may help the transplant to "take" faster.
Detailed description
PRIMARY OBJECTIVES: I. To evaluate the safety and feasibility of transplantation of cord blood which is expanded in mesenchymal precursor cell (MPC) co-cultures then fucosylated with fucosyltransferase (FT)-VI and guanosine diphosphate (GDP) fucose prior to infusion in patients with hematologic malignancies following high-dose therapy. II. To evaluate the time to engraftment using expanded fucosylated cord blood. SECONDARY OBJECTIVES: I. To evaluate the rate and severity of graft versus host disease. II. To evaluate the rates of infectious complications. III. To evaluate the rates of disease-free and overall survival. Summary: All patients receive Busulfan as per standard of care. Busulfan test dose can be administered either as an outpatient prior to admission or as an inpatient on Day -10. Busulfan pharmacokinetics will be performed with the test dose and the first dose on Day -7 per standard of care. The doses of Days -6, -5, and -4 will be subsequently adjusted to target an AUC of 4,000 microMol.min-1. In the event that PK adjusting were not possible a dose of busulfan of 130 mg/m2 will be administered. GVHD PROPHYLAXIS: All patients receive mycofenolate mofetil IV over 2 hours or orally (PO) twice daily (BID) on days -3 with a taper beginning on day 100 in the absence of GVHD, tacrolimus IV or PO starting on day -2 for 6 months in the absence of GVHD, and filgrastim-sndz subcutaneously (SC) once daily (QD) starting on day 0 until white blood count begins to recover. After completion of study treatment, patients are followed up at months 1, 3, 6, and 12.
Conditions
- Accelerated Phase Chronic Myelogenous Leukemia, BCR-ABL1 Positive
- Acute Biphenotypic Leukemia
- Acute Leukemia
- Acute Lymphoblastic Leukemia
- Acute Lymphoblastic Leukemia in Remission
- Acute Myeloid Leukemia
- Acute Myeloid Leukemia Arising From Previous Myelodysplastic Syndrome
- Chemotherapy-Related Leukemia
- Chronic Lymphocytic Leukemia
- Chronic Myelogenous Leukemia, BCR-ABL1 Positive
- Chronic Myelomonocytic Leukemia
- Hodgkin Lymphoma
- Langerhans Cell Histiocytosis
- Minimal Residual Disease
- Myelodysplastic Syndrome
- Myelodysplastic Syndrome With Excess Blasts
- Non-Hodgkin Lymphoma
- Recurrent Hodgkin Lymphoma
- Refractory Acute Lymphoblastic Leukemia
- Refractory Myelodysplastic Syndrome
- Small Lymphocytic Lymphoma
- Therapy-Related Myelodysplastic Syndrome
Interventions
| Type | Name | Description |
|---|---|---|
| BIOLOGICAL | Anti-Thymocyte Globulin | Given IV |
| DRUG | Busulfan | Given IV |
| DRUG | Clofarabine | Given IV |
| DRUG | Cyclophosphamide | Given IV |
| BIOLOGICAL | Filgrastim-sndz | Given SC |
| DRUG | Fludarabine | Given IV |
| DRUG | Melphalan | Given IV |
| DRUG | Mycophenolate Mofetil | Given IV or PO |
| BIOLOGICAL | Rituximab | Given IV |
| DRUG | Tacrolimus | Given IV |
| RADIATION | Total-Body Irradiation | Undergo total body irradiation |
| PROCEDURE | Umbilical Cord Blood Transplantation | Undergo cord blood transplant |
Timeline
- Start date
- 2017-10-13
- Primary completion
- 2022-09-20
- Completion
- 2022-09-20
- First posted
- 2017-03-30
- Last updated
- 2023-10-11
- Results posted
- 2023-06-28
Locations
1 site across 1 country: United States
Regulatory
- FDA-regulated drug study
Source: ClinicalTrials.gov record NCT03096782. Inclusion in this directory is not an endorsement.