Trials / Recruiting
RecruitingNCT02998710
Natural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)
A Multicenter, Observational, Prospective, Natural History Study of Homocystinuria Due to Cystathionine Beta-synthase Deficiency in Pediatric and Adult Patients (ACAPPELLA)
- Status
- Recruiting
- Phase
- —
- Study type
- Observational
- Enrollment
- 150 (estimated)
- Sponsor
- Travere Therapeutics, Inc. · Industry
- Sex
- All
- Age
- 1 Year – 65 Years
- Healthy volunteers
- Not accepted
Summary
The purpose of the study is to characterize the clinical course of homocystinuria in pediatric and adult patients aged 1 to 65 years under current clinical management practices
Conditions
Timeline
- Start date
- 2017-01-01
- Primary completion
- 2026-04-01
- Completion
- 2026-08-01
- First posted
- 2016-12-20
- Last updated
- 2024-11-22
Locations
11 sites across 4 countries: United States, Ireland, Qatar, United Kingdom
Source: ClinicalTrials.gov record NCT02998710. Inclusion in this directory is not an endorsement.