Trials / Unknown
UnknownNCT02520934
Miglustat on Gaucher Disease Type IIIB
Evaluation of Combination Therapy With Miglustat and Enzyme Replacement Therapy on Gaucher Disease Type IIIB
- Status
- Unknown
- Phase
- N/A
- Study type
- Interventional
- Enrollment
- 19 (actual)
- Sponsor
- National Taiwan University Hospital · Academic / Other
- Sex
- All
- Age
- 6 Years
- Healthy volunteers
- Accepted
Summary
evaluate the combination therapy with Miglustat and enzyme replacement therapy (ERT) on Gaucher disease
Detailed description
understand if Miglustat (glucosylceramide synthase inhibitor) could improve neuropathy in patients with Gaucher disease
Conditions
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | Miglustat | combine miglustat and ERT to see if neurologic manifestations can be improved |
| DRUG | ERT | enzyme replacement therapy |
Timeline
- Start date
- 2015-07-01
- Primary completion
- 2017-12-01
- Completion
- 2019-12-01
- First posted
- 2015-08-13
- Last updated
- 2019-03-29
Locations
1 site across 1 country: Taiwan
Source: ClinicalTrials.gov record NCT02520934. Inclusion in this directory is not an endorsement.