Trials / Terminated
TerminatedNCT02293408
Natural History Study to Characterise the Course of Disease Progression in Participants With Mucopolysaccharidosis Type IIIB
A Prospective Cross-Sectional and Longitudinal Study With Additional Retrospective Chart Review to Evaluate Clinical and Biochemical Characteristics and Disease Progression in Patients With Mucopolysaccharidosis Type IIIB
- Status
- Terminated
- Phase
- —
- Study type
- Observational
- Enrollment
- 30 (actual)
- Sponsor
- Alexion Pharmaceuticals, Inc. · Industry
- Sex
- All
- Age
- 1 Year
- Healthy volunteers
- Not accepted
Summary
The objectives of this study are to describe the clinical and biochemical characteristics and course of disease progression in participants with Mucopolysaccharidosis type IIIB (MPS IIIB)
Conditions
Timeline
- Start date
- 2014-09-14
- Primary completion
- 2017-07-11
- Completion
- 2017-07-11
- First posted
- 2014-11-18
- Last updated
- 2018-09-13
Locations
7 sites across 6 countries: United States, Brazil, Italy, Portugal, Spain, United Kingdom
Source: ClinicalTrials.gov record NCT02293408. Inclusion in this directory is not an endorsement.