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Trials / Completed

CompletedNCT01981837

Phase 2 Study to Evaluate ALN-TTRSC (Revusiran) in Patients With Transthyretin (TTR) Cardiac Amyloidosis

A Phase 2, Open-Label Trial to Evaluate the Safety, Pharmacokinetics, Pharmacodynamics and Exploratory Clinical Activity of ALN-TTRSC in Patients With Transthyretin (TTR) Cardiac Amyloidosis

Status
Completed
Phase
Phase 2
Study type
Interventional
Enrollment
26 (actual)
Sponsor
Alnylam Pharmaceuticals · Industry
Sex
All
Age
18 Years – 80 Years
Healthy volunteers
Not accepted

Summary

The purpose of this study is to determine the pharmacokinetics, pharmacodynamics and exploratory clinical activity of ALN-TTRSC (revusiran) in Patients with Transthyretin (TTR) Cardiac Amyloidosis.

Conditions

Interventions

TypeNameDescription
DRUGALN-TTRSC (revusiran) for subcutaneous administration

Timeline

Start date
2013-12-01
Primary completion
2014-10-01
Completion
2015-01-01
First posted
2013-11-13
Last updated
2023-03-20

Locations

4 sites across 2 countries: United States, United Kingdom

Source: ClinicalTrials.gov record NCT01981837. Inclusion in this directory is not an endorsement.

Phase 2 Study to Evaluate ALN-TTRSC (Revusiran) in Patients With Transthyretin (TTR) Cardiac Amyloidosis (NCT01981837) · Clinical Trials Directory