Clinical Trials Directory

Trials / Unknown

UnknownNCT01954953

Clinical and Genetic Examination of Usher Syndrome Patients' Cohort in Europe

European Research Projects on Rare Diseases Driven by Young Investigators

Status
Unknown
Phase
Study type
Observational
Enrollment
100 (estimated)
Sponsor
Centre Hospitalier National d'Ophtalmologie des Quinze-Vingts · Academic / Other
Sex
All
Age
6 Months – 70 Years
Healthy volunteers
Not accepted

Summary

This study aims to characterize Usher patients in order to correlate this data with genetic information. Tasks: * Standardization and improvement of Usher syndrome diagnosis: refine and elaborate special tests of visual and otological function in association with genotype that enable to determine the most significant markers for Usher disease progression and therapeutic effect. * Perform genotype and phenotype correlations in Usher syndrome patients * Develop and maintain database for phenotypically and genotypically well-characterized patient cohorts, suitable for future therapeutic trials

Conditions

Timeline

Start date
2013-09-01
Primary completion
2016-01-01
First posted
2013-10-07
Last updated
2015-02-04

Locations

6 sites across 4 countries: France, Germany, Netherlands, Portugal

Source: ClinicalTrials.gov record NCT01954953. Inclusion in this directory is not an endorsement.