Trials / Completed
CompletedNCT01760564
Application of Miglustat in Patients With Niemann-Pick Type C
- Status
- Completed
- Phase
- Phase 3
- Study type
- Interventional
- Enrollment
- 5 (actual)
- Sponsor
- National Taiwan University Hospital · Academic / Other
- Sex
- All
- Age
- —
- Healthy volunteers
- Not accepted
Summary
To evaluate the changes in cognitive function after miglustat treatment in Niemann-Pick type C patients.
Detailed description
Patients with Niemann-Pick C disease will be treated with Miglutat 200mg tid. Neurologic evaluation and safety will be monitored periodically.
Conditions
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | Miglustat | miglustat 200mg tid for adult. For children surface area correction will be made. A lower dose may be used initially to decrease side effect. |
Timeline
- Start date
- 2008-01-01
- Primary completion
- 2010-12-01
- Completion
- 2010-12-01
- First posted
- 2013-01-04
- Last updated
- 2013-01-04
Locations
1 site across 1 country: Taiwan
Source: ClinicalTrials.gov record NCT01760564. Inclusion in this directory is not an endorsement.