Clinical Trials Directory

Trials / Completed

CompletedNCT00790127

Phase 1/2 Study of HQK-1001 in Patients With Beta Thalassemia

A Multi-National, Blinded, Placebo-Controlled, Dose Escalation Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of HQK-1001 in Subjects With Beta Thalassemia Intermedia, Including Hemoglobin E Beta Thalassemia

Status
Completed
Phase
Phase 1 / Phase 2
Study type
Interventional
Enrollment
21 (actual)
Sponsor
HemaQuest Pharmaceuticals Inc. · Industry
Sex
All
Age
12 Years – 60 Years
Healthy volunteers
Not accepted

Summary

The purpose of this study is to evaluate the safety and tolerability of HQK-1001 administered daily for 8 weeks in subjects with beta thalassemia intermedia

Conditions

Interventions

TypeNameDescription
DRUGHQK-1001HQK-1001 capsules (10, 20, 30 or 40 mg) administered once a day, orally, for 56 days
DRUGPlaceboMatching placebo capsules administered once a day, orally, for 56 days

Timeline

Start date
2009-03-01
Primary completion
2010-05-01
Completion
2010-05-01
First posted
2008-11-13
Last updated
2011-05-20

Locations

2 sites across 2 countries: Lebanon, Thailand

Source: ClinicalTrials.gov record NCT00790127. Inclusion in this directory is not an endorsement.