Trials / Completed
CompletedNCT00048711
Open-Label Study of Efficacy and Safety of Recombinant Human N-acetylgalactosamine 4-sulfatase in Patients With MPS VI
- Status
- Completed
- Phase
- Phase 2
- Study type
- Interventional
- Enrollment
- —
- Sponsor
- BioMarin Pharmaceutical · Industry
- Sex
- All
- Age
- 5 Years
- Healthy volunteers
- Not accepted
Summary
The purpose of the study is evaluate the efficacy, safety, and pharmacokinetics of weekly intravenous infusions of 1 mg/kg recombinant human N-acetylgalactosamine 4-sulfatase (rhASB) in patients diagnosed with Mucopolysaccharidosis VI (MPS VI)
Conditions
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | N-acetylgalactosamine 4-sulfatase |
Timeline
- Start date
- 2002-03-01
- Completion
- 2006-06-01
- First posted
- 2002-11-08
- Last updated
- 2009-08-25
Locations
1 site across 1 country: United States
Source: ClinicalTrials.gov record NCT00048711. Inclusion in this directory is not an endorsement.