Clinical Trials Directory

Trials / Sponsors / University Research Foundation for Lysosomal Storage Diseases, Inc.

University Research Foundation for Lysosomal Storage Diseases, Inc.

Academic / Other · 1 registered clinical trial.

StatusTrialPhaseStarted
CompletedValidating a New Severity Score System for Adults With Type 1 Gaucher Disease (GD1)
Gaucher Disease
2010-04-01