Clinical Trials Directory

Trials / Sponsors / UniQure Biopharma B.V.

UniQure Biopharma B.V.

Industry · 8 registered clinical trials — 2 currently recruiting.

StatusTrialPhaseStarted
Active Not RecruitingSafety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adu
Amyotrophic Lateral Sclerosis
Phase 1 / Phase 22024-08-01
RecruitingAMT-260 Gene Therapy Study in Adults With Unilateral Refractory Mesial Temporal Lobe Epilepsy
Mesial Temporal Lobe Epilepsy
Phase 1 / Phase 22024-06-12
RecruitingSafety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease
Fabry Disease
Phase 1 / Phase 22024-06-05
Active Not RecruitingSafety and Efficacy of AMT-130 in European Adults With Early Manifest Huntington's Disease
Huntington Disease
Phase 1 / Phase 22021-10-07
Active Not RecruitingSafety and Proof-of-Concept (POC) Study With AMT-130 in Adults With Early Manifest Huntington's Disease
Huntington's Disease
Phase 1 / Phase 22019-09-06
WithdrawnAlipogene Tiparvovec for the Treatment of LPLD Patients
LPL Deficiency
Phase 22016-10-01
CompletedGlybera Registry, Lipoprotein Lipase Deficient (LPLD) Patients
Lipoprotein Lipase Deficiency, Familial Hyperlipoproteinemia Type 1, Familial Hyperchylomicronemia
—2014-06-27
CompletedIntracerebral Gene Therapy in Children With Sanfilippo Type B Syndrome
Sanfilippo Syndrome B
Phase 1 / Phase 22013-09-17