Clinical Trials Directory

Trials / Sponsors / Terence Flotte

Terence Flotte

Academic / Other · 2 registered clinical trials.

StatusTrialPhaseStarted
Active Not RecruitingLong-Term Follow-Up of Subjects Treated With AXO-AAV-GM2 for Tay-Sachs or Sandhoff Disease
GM2 Gangliosidosis, Tay Sachs Disease, Sandhoff Disease
2024-09-17
TerminatedA Dose-escalation and Safety & Efficacy Study of AXO-AAV-GM2 in Tay-Sachs or Sandhoff Disease
Tay-Sachs Disease, Sandhoff Disease
Phase 12021-01-15