Trials / Sponsors / Rare Disease Research, LLC
Rare Disease Research, LLC
Academic / Other · 1 registered clinical trial.
| Status | Trial | Phase | Started |
|---|---|---|---|
| Terminated | An Open-Label Study of Golodirsen in Non-Ambulant Patients With Duchenne Muscular Dystrophy Duchenne Muscular Dystrophy | Phase 4 | 2020-10-31 |