Clinical Trials Directory

Trials / Sponsors / Novartis Gene Therapies

Novartis Gene Therapies

Industry · 8 registered clinical trials.

StatusTrialPhaseStarted
Active Not RecruitingLong-term Follow-up Study of Patients Receiving Onasemnogene Abeparvovec-xioi
Spinal Muscular Atrophy Type I, Spinal Muscular Atrophy Type II, Spinal Muscular Atrophy Type III
Phase 32020-02-10
CompletedSingle-Dose Gene Replacement Therapy Using for Patients With Spinal Muscular Atrophy Type 1 With One or Two SM
Spinal Muscular Atrophy Type I
Phase 32019-05-31
CompletedSingle-Dose Gene Replacement Therapy Clinical Trial for Participants With Spinal Muscular Atrophy Type 1
SMA
Phase 32018-08-16
CompletedPre-Symptomatic Study of Intravenous Onasemnogene Abeparvovec-xioi in Spinal Muscular Atrophy (SMA) for Patien
Spinal Muscular Atrophy
Phase 32018-04-02
TerminatedStudy of Intrathecal Administration of Onasemnogene Abeparvovec-xioi for Spinal Muscular Atrophy
Spinal Muscular Atrophy
Phase 12017-12-14
CompletedGene Replacement Therapy Clinical Trial for Participants With Spinal Muscular Atrophy Type 1
SMA - Spinal Muscular Atrophy, Gene Therapy
Phase 32017-10-24
Active Not RecruitingLong-Term Follow-up Study for Patients From AVXS-101-CL-101
Spinal Muscular Atrophy 1
—2017-09-21
CompletedGene Transfer Clinical Trial for Spinal Muscular Atrophy Type 1
Spinal Muscular Atrophy 1
Phase 12014-05-05