Trials / Sponsors / Megan Waldrop
Megan Waldrop
Academic / Other · 2 registered clinical trials — 1 currently recruiting.
| Status | Trial | Phase | Started |
|---|---|---|---|
| Enrolling By Invitation | Gene Therapy for IGHMBP2-Related Diseases SMARD1, CMT2S | Phase 1 / Phase 2 | 2021-11-04 |
| Completed | AAV9 U7snRNA Gene Therapy to Treat Boys With DMD Exon 2 Duplications. Duchenne Muscular Dystrophy | Phase 1 / Phase 2 | 2020-01-15 |