LYSOGENE
Industry · 6 registered clinical trials.
| Status | Trial | Phase | Started |
|---|---|---|---|
| Terminated | A Safety and Efficacy Study of LYS-GM101 Gene Therapy in Patients With GM1 Gangliosidosis GM1 Gangliosidosis | Phase 1 / Phase 2 | 2021-05-11 |
| Completed | Interviews and Video Capture in Patients With GM1 Gangliosidosis GM1 Gangliosidosis | — | 2020-04-20 |
| Unknown | Study of AAVrh10-h.SGSH Gene Therapy in Patients With Mucopolysaccharidosis Type IIIA (MPS IIIA) Mucopolysaccharidosis Type IIIA | Phase 2 / Phase 3 | 2018-12-17 |
| Completed | Natural History Study of Patients With MPS IIIA Mucopolysaccharidosis IIIA | — | 2016-04-01 |
| Completed | Long-term Follow-up of Sanfilippo Type A Patients Treated by Intracerebral SAF-301 Gene Therapy Mucopolysaccharidosis Type III A, Sanfilippo Disease Type A | Phase 1 / Phase 2 | 2013-05-01 |
| Completed | Intracerebral Gene Therapy for Sanfilippo Type A Syndrome Mucopolysaccharidosis Type III A, Sanfilippo Disease Type A | Phase 1 / Phase 2 | 2011-08-01 |