Clinical Trials Directory

Trials / Sponsors / Jaguar Gene Therapy, LLC

Jaguar Gene Therapy, LLC

Industry · 1 registered clinical trial1 currently recruiting.

StatusTrialPhaseStarted
RecruitingJAG201 Gene Therapy Study in Children & Adults With SHANK3 Haploinsufficiency
SHANK3 Haploinsufficiency, Phelan-McDermid Syndrome
Phase 1 / Phase 22024-01-07