Clinical Trials Directory

Trials / Sponsors / HuidaGene Therapeutics Co., Ltd.

HuidaGene Therapeutics Co., Ltd.

Industry · 7 registered clinical trials5 currently recruiting.

StatusTrialPhaseStarted
RecruitingAn Clinical Study Evaluating the Safety, Tolerability, and efficAcy of HG005 in StaRgardT Disease
Stargardt Disease Type 1 (STGD1)
EARLY_Phase 12025-08-20
Not Yet RecruitingOpen-laBel Dose-escalation Study for CRISPR/cas13- Rna TargetInG THerapy for the Treatment of Neovascular Age-
Neovascular Age-Related Macular Degeneration (nAMD)
Phase 12025-04-01
CompletedAn Open-label, Multidose Dose-escalation Study to Understand the Safety of CRISPR Gene-editing Therapy and Its
Duchenne Muscular Dystrophin (DMD)
EARLY_Phase 12024-11-06
RecruitingA First-in-Human Clinical Trial to Evaluate the Safety, Tolerability, and Efficacy of a Novel CRISPR RNA-editi
MECP2 Duplication Syndrome
N/A2024-10-30
RecruitingSafety and Efficacy Trial of HG004 for Leber Congenital Amaurosis Related to Rpe65 Gene Mutations (STAR)
Leber Congenital Amaurosis, Inherited Retinal Diseases Caused by RPE65 Mutations
Phase 1 / Phase 22023-10-31
RecruitingCRISPR/cas13-medIated RNA TarGeting THerapy for the Treatment of Neovascular Age-related Macular Degeneration
Neovascular Age-related Macular Degeneration(nAMD)
EARLY_Phase 12023-09-04
Withdrawna Study in Subjects With Otoferlin Mutation-related Hearing Loss Using RNA Base-eDiting Therapy(SOUND)
Congenital Hearing Loss
EARLY_Phase 12023-03-30