Trials / Sponsors / Gemma Biotherapeutics
Gemma Biotherapeutics
Industry · 3 registered clinical trials — 1 currently recruiting.
| Status | Trial | Phase | Started |
|---|---|---|---|
| Recruiting | Study of Safety, Tolerability and Efficacy of GB221 in Infants With Spinal Muscular Atrophy Type 1 Spinal Muscular Atrophy Type I | Phase 1 / Phase 2 | 2026-01-06 |
| Suspended | Study of Safety, Tolerability and Efficacy of PBKR03 in Pediatric Subjects With Early Infantile Krabbe Disease Leukodystrophy, Globoid Cell | Phase 1 / Phase 2 | 2022-02-24 |
| Active Not Recruiting | Study of Safety, Tolerability and Efficacy of PBGM01 in Pediatric Participants With GM1 Gangliosidosis GM1 Gangliosidosis, GM1 Gangliosidosis, Type I, GM1 Gangliosidosis, Type 2 | Phase 1 / Phase 2 | 2021-03-17 |