Clinical Trials Directory

Trials / Sponsors / Emily de los Reyes

Emily de los Reyes

Academic / Other · 5 registered clinical trials1 currently recruiting.

StatusTrialPhaseStarted
Enrolling By InvitationGene Therapy for SLC6A1 Neurodevelopmental Disorder
SLC6A1
Phase 1 / Phase 22025-08-25
TerminatedNatural History Study of Batten Disease
Batten Disease, Neuronal Ceroid Lipofuscinosis CLN6, Neuronal Ceroid Lipofuscinosis CLN3
2021-04-27
Active Not RecruitingLong-Term Follow Up of CLN6 Batten Disease Subjects Following Gene Transfer
CLN6, Batten Disease
2020-01-24
Active Not RecruitingNatural History of Neuronal Ceroid Lipofuscinosis, Batten's CLN6 Diseae
Batten Disease, CLN6
2017-01-01
CompletedGene Therapy For Children With Variant Late Infantile Neuronal Ceroid Lipofuscinosis 6 (vLINCL6) Disease
Variant Late-Infantile Neuronal Ceroid Lipofuscinosis
Phase 1 / Phase 22016-05-01