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Trials / Sponsors / Elpida Therapeutics SPC

Elpida Therapeutics SPC

Industry · 4 registered clinical trials4 currently recruiting.

StatusTrialPhaseStarted
Not Yet RecruitingStudy of Intrathecal ELP-02 for Charcot-Marie-Tooth Disease Type 4J (CMT4J)
Charcot-Marie-Tooth Disease Type 4J
Phase 1 / Phase 22026-04-01
RecruitingPhase 3 Efficacy Study With Concurrent Control of IT MELPIDA in SPG50.Concurrent Controls.
Hereditary Spastic Paraplegia Type 50
Phase 32026-02-01
RecruitingA Prospective Natural History and Outcome Measure Discovery Study of Charcot-Marie-Tooth Disease, Type 4J
Peripheral Neuropathy, Neuro-Degenerative Disease, Neuromuscular Diseases
2024-07-29
RecruitingMelpida: Recombinant Adeno-associated Virus (serotype 9) Encoding a Codon Optimized Human AP4M1 Transgene (hAP
Spasticity, Muscle, Microcephaly, Intellectual Deficiency
Phase 1 / Phase 22023-02-15