Clinical Trials Directory

Trials / Sponsors / Clinic for Special Children

Clinic for Special Children

Academic / Other · 2 registered clinical trials1 currently recruiting.

StatusTrialPhaseStarted
Active Not RecruitingRisdiplam in Patients With Spinal Muscular Atrophy Previously Treated With Nusinersen
Spinal Muscular Atrophy
Phase 42022-11-06
RecruitingWiTNNess - TNNT1 Myopathy Natural History Study
TNNT1-associated Myopathy, Infantile-onset Nemaline Rod Myopathy, Myopathies, Nemaline
2018-09-23