Clinical Trials Directory

Trials / Sponsors / Bioblast Pharma Ltd.

Bioblast Pharma Ltd.

Industry · 5 registered clinical trials.

StatusTrialPhaseStarted
WithdrawnTreatment of Oculopharyngeal Muscular Dystrophy With Trehalose
Oculopharyngeal Muscular Dystrophy
Phase 22017-06-15
CompletedA Study to Establish Safety and Maximum Tolerated Dose of IV Trehalose in Healthy Subjects
Healthy Volunteer Subjects
Phase 12016-03-01
CompletedContinuation Protocol to Protocol BBCO-001
Muscular Dystrophy, Oculopharyngeal (OPMD)
Phase 32015-01-01
CompletedStudy To Assess Safety, Tolerability and Efficacy of Intravenous Cabaletta in Patients With Machado-Joseph Dis
Machado-Joseph Disease / Spinocerebellar Ataxia 3
Phase 22014-07-01
CompletedSafety Tolerability and Efficacy Study of Cabaletta to Treat Oculopharyngeal Muscular Dystrophy (OPMD) Patient
Oculopharyngeal Muscular Dystrophy
Phase 22014-02-01