Trials / Sponsors / Beyond Batten Disease Foundation
Beyond Batten Disease Foundation
Academic / Other · 1 registered clinical trial.
| Status | Trial | Phase | Started |
|---|---|---|---|
| Completed | An Open-label Safety, Pharmacokinetic, and Efficacy Study of Miglustat for the Treatment of Subjects With Batt Batten Disease | Phase 1 / Phase 2 | 2022-03-10 |