Trials / Conditions / Zellweger Syndrome
Zellweger Syndrome
6 registered clinical trials studyying Zellweger Syndrome — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Completed | Hydroxychloroquine Administration for Reduction of Pexophagy NCT03856866 | The Hospital for Sick Children | Phase 2 |
| Completed | LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies NCT02699190 | Children's Hospital of Philadelphia | — |
| Recruiting | The Myelin Disorders Biorepository Project NCT03047369 | Children's Hospital of Philadelphia | — |
| Active Not Recruiting | MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis NCT02171104 | Masonic Cancer Center, University of Minnesota | Phase 2 |
| Completed | Compassionate Treatment of Patients With Inborn Errors of Bile Acid Metabolism With Cholic Acid NCT00007020 | Mirum Pharmaceuticals, Inc. | Phase 3 |
| Terminated | Study of Bile Acids in Patients With Peroxisomal Disorders NCT00004442 | University of Cincinnati | N/A |