Clinical Trials Directory

Trials / Conditions / Wolfram Syndrome

Wolfram Syndrome

11 registered clinical trials studyying Wolfram Syndrome3 currently recruiting.

StatusTrialSponsorPhase
Not Yet RecruitingMechanisms of Fecal Incontinence in Wolfram Syndrome
NCT07313085
Hôpital Necker-Enfants Malades
UnknownTirzepatide Monotherapy in Patients With Wolfram Syndrome Type 1
NCT05659368
Ospedale San RaffaelePhase 2
Active Not RecruitingAMX0035 in Adult Patients With Wolfram Syndrome
NCT05676034
Amylyx Pharmaceuticals Inc.Phase 2
UnknownEfficacy Study of Daily Administration of VPA in Patients Affected by Wolfram Syndrome
NCT04940572
Centre d'Etude des Cellules SouchesPhase 2
RecruitingMonogenic Diabetes Misdiagnosed as Type 1
NCT03988764
McGill University Health Centre/Research Institute of the McGill University Health Centre
Active Not RecruitingEfficacy and Safety Trial of Sodium Valproate, in Paediatric and Adult Patients With Wolfram Syndrome
NCT03717909
University of BirminghamPhase 2
CompletedI-Tracking Neurodegeneration in Early Wolfram Syndrome
NCT03951298
Washington University School of Medicine
CompletedA Clinical Trial of Dantrolene Sodium in Pediatric and Adult Patients With Wolfram Syndrome
NCT02829268
Washington University School of MedicinePhase 1 / Phase 2
CompletedTracking Neurodegeneration in Early Wolfram Syndrome
NCT02455414
Washington University School of Medicine
RecruitingWolfram Syndrome and WFS1-related Disorders International Registry and Clinical Study
NCT02841553
Washington University School of Medicine
WithdrawnGLP Analogs for Diabetes in Wolfram Syndrome Patients
NCT01302327
Hadassah Medical OrganizationN/A