Trials / Conditions / TUBB4A-Related Leukodystrophy
TUBB4A-Related Leukodystrophy
3 registered clinical trials studyying TUBB4A-Related Leukodystrophy — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Active Not Recruiting | An Open-label, Single Center, Single Participant Study of an Experimental Antisense Oligonucleotide Treatment NCT07222371 | University of California, San Diego | Phase 1 / Phase 2 |
| Completed | LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies NCT02699190 | Children's Hospital of Philadelphia | — |
| Recruiting | The Myelin Disorders Biorepository Project NCT03047369 | Children's Hospital of Philadelphia | — |