Trials / Conditions / Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy
Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy
4 registered clinical trials studyying Transthyretin-Related (ATTR) Familial Amyloid Cardiomyopathy — 2 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | Long-Term Follow-Up (LTFU) of Subjects Dosed With NTLA-2001 NCT05697861 | Intellia Therapeutics | — |
| Recruiting | Subclinical Transthyretin Cardiac Amyloidosis in V122I TTR Carriers NCT05489549 | University of Texas Southwestern Medical Center | — |
| Completed | Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of NTLA-2001 in Patients With H NCT04601051 | Intellia Therapeutics | Phase 1 |
| Completed | TRAMmoniTTR Study Genetic Screening of an At-risk Population for hATTR and Monitoring of TTR Positive Subjects NCT03237494 | CENTOGENE GmbH Rostock | — |