Clinical Trials Directory

Trials / Conditions / Transfusion Dependent Beta-Thalassaemia

Transfusion Dependent Beta-Thalassaemia

4 registered clinical trials studyying Transfusion Dependent Beta-Thalassaemia1 currently recruiting.

StatusTrialSponsorPhase
RecruitingHematopoietic Stem Cell BCL11A Enhancer Gene Editing for Severe β-Hemoglobinopathies
NCT06647979
Daniel BauerPhase 1
TerminatedA Study to Evaluate the Safety and Efficacy of ET-01 Transplantation in Subjects with Transfusion Dependent Β-
NCT05752123
EdiGene (GuangZhou) Inc.N/A
CompletedSafety and Efficacy Evaluation of ET-01 Transplantation in Subjects With Transfusion Dependent β-Thalassaemia
NCT04390971
Institute of Hematology & Blood Diseases Hospital, ChinaN/A
TerminatedA Safety and Efficacy Study Evaluating ET-01 in Subjects with Transfusion Dependent Β-Thalassaemia
NCT04925206
EdiGene (GuangZhou) Inc.Phase 1