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Trials / Conditions / Tetrahydrobiopterin Deficiency

Tetrahydrobiopterin Deficiency

3 registered clinical trials studyying Tetrahydrobiopterin Deficiency.

StatusTrialSponsorPhase
WithdrawnO2 Transport and Utilization in Health and Lung Disease
NCT04014712
University of Massachusetts, AmherstPhase 1
CompletedAcceptability and Tolerance of a Ready-to-use Protein Substitute in Tablet Form for the Dietary Management of
NCT04375592
metaX Institut fuer Diatetik GmbH
CompletedRetrospective Observational Safety Effectiveness With Kuvan in hpA
NCT03864029
BioMarin Pharmaceutical