Trials / Conditions / Sanfilippo A
Sanfilippo A
3 registered clinical trials studyying Sanfilippo A — 2 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Enrolling By Invitation | Follow-up Study of AAV-Mediated Gene Transfer (UX111; Previously Known as ABO-102) for MPS Type IIIA NCT04360265 | Ultragenyx Pharmaceutical Inc | Phase 3 |
| Terminated | Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease NCT04088734 | Ultragenyx Pharmaceutical Inc | Phase 1 / Phase 2 |
| Recruiting | Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH NCT02716246 | Ultragenyx Pharmaceutical Inc | Phase 2 / Phase 3 |