Clinical Trials Directory

Trials / Conditions / Refsum Disease

Refsum Disease

3 registered clinical trials studyying Refsum Disease2 currently recruiting.

StatusTrialSponsorPhase
CompletedLeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies
NCT02699190
Children's Hospital of Philadelphia
RecruitingThe Myelin Disorders Biorepository Project
NCT03047369
Children's Hospital of Philadelphia
RecruitingRare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT01793168
Sanford Health