Trials / Conditions / PAH Deficiency
PAH Deficiency
4 registered clinical trials studyying PAH Deficiency — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Terminated | Safety and Efficacy of HMI-103 in Participants With Classical PKU Due to PAH Deficiency NCT05222178 | Homology Medicines, Inc | Phase 1 |
| Enrolling By Invitation | Long-Term Follow Up Study of Subjects Previously Administered HMI 102 NCT04348708 | Homology Medicines, Inc | — |
| Unknown | BH4 Responsiveness in PAH Deficiency PKU Patients NCT04227080 | Taipei Veterans General Hospital, Taiwan | Phase 4 |
| Terminated | Gene Therapy Clinical Study in Adult PKU NCT03952156 | Homology Medicines, Inc | Phase 1 / Phase 2 |