Trials / Conditions / OTC Deficiency
OTC Deficiency
4 registered clinical trials studyying OTC Deficiency — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | A Study to Evaluate the Pharmacodynamics and Safety of ARCT-810 in Participants With OTCD NCT06488313 | Arcturus Therapeutics, Inc. | Phase 2 |
| Active Not Recruiting | Clinical Study of DTX301 AAV-Mediated Gene Transfer for Ornithine Transcarbamylase (OTC) Deficiency NCT05345171 | Ultragenyx Pharmaceutical Inc | Phase 3 |
| Terminated | Study for Adolescents and Adults With Ornithine Transcarbamylase Deficiency to Evaluate Safety and Tolerabilit NCT05526066 | Arcturus Therapeutics, Inc. | Phase 2 |
| Completed | Patient and Observer Reported Outcome Measurements in Inborn Errors of Metabolism NCT04248062 | University Children's Hospital, Zurich | — |