Trials / Conditions / Ornithine Transcarbamylase Deficiency Disease

Ornithine Transcarbamylase Deficiency Disease

4 registered clinical trials studyying Ornithine Transcarbamylase Deficiency Disease — 2 currently recruiting.

Status	Trial	Sponsor	Phase
Recruiting	Long-term Follow-up (LTFU) Study of Participants in Any iECURE Protocol Using an Investigational Product (IP) NCT06805695	iECURE, Inc.	—
Recruiting	An Open-label Study to Investigate ECUR-506 in Male Babies Less Than 9 Months of Age With Neonatal Onset OTC D NCT06255782	iECURE, Inc.	Phase 1 / Phase 2
Terminated	Phase I Study of Adenoviral Vector Mediated Gene Transfer for Ornithine Transcarbamylase in Adults With Partia NCT00004498	University of Pennsylvania	Phase 1
Terminated	Phase I Pilot Study of Liver-Directed Gene Therapy for Partial Ornithine Transcarbamylase Deficiency NCT00004386	Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)	Phase 1