Clinical Trials Directory

Trials / Conditions / Non-transfusion-dependent Thalassemia

Non-transfusion-dependent Thalassemia

7 registered clinical trials studyying Non-transfusion-dependent Thalassemia.

StatusTrialSponsorPhase
CompletedEffect of L-Glutamine on Pulmonary Artery Pressure in Patients With Non-Transfusion-Dependent Thalassemia
NCT07210450
Mazandaran University of Medical SciencesPhase 2 / Phase 3
CompletedA Study Investigate the Safety, Tolerability, Pharmacokinetic, and Pharmacodynamic Response of SLN124 in Adult
NCT04718844
Silence Therapeutics plcPhase 1
CompletedSafety, Tolerability, Pharmacokinetics (PK), Pharmacodynamics (PD) and Preliminary Efficacy of VIT-2763 in β-t
NCT04364269
Vifor (International) Inc.Phase 2
WithdrawnStudy in Beta-thalassaemia or Myelodysplastic Syndrome Patients to Investigate the Safety and Tolerability of
NCT04176653
Silence Therapeutics plcPhase 1
CompletedOpen-label, Multicenter Study Assessing Preference for Deferasirox Film-coated Tablet Compared to Dispersible
NCT02993224
Novartis PharmaceuticalsPhase 2
CompletedEfficacy and Safety Study of Deferasirox in Patients With Non-transfusion Dependent Thalassemia
NCT01709838
Novartis PharmaceuticalsPhase 4
CompletedEfficacy and Safety of Deferasirox in Non-transfusion Dependent Thalassemia Patients With Iron Overload and a
NCT00873041
Novartis PharmaceuticalsPhase 2