Clinical Trials Directory

Trials / Conditions / Niemann-Pick Disease, Type C1

Niemann-Pick Disease, Type C1

9 registered clinical trials studyying Niemann-Pick Disease, Type C1 — 1 currently recruiting.

StatusTrialSponsorPhase
CompletedFunctional Near-Infrared Spectroscopy (fNIRS) Combined With Diffuse Correlation Spectroscopy (DCS) in Neurocog
NCT05642221
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)—
Active Not RecruitingPhase 3 Study to Evaluate Intravenous Trappsol(R) Cyclo(TM) in Pediatric and Adult Patients With Niemann-Pick
NCT04860960
Cyclo Therapeutics, Inc.Phase 3
TerminatedCombined Intrathecal and Intravenous VTS-270 Therapy for Liver and Neurological Disease Associated With Nieman
NCT03887533
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)Phase 1 / Phase 2
UnknownOpen-Label Study of Long-Term Safety and Efficacy of Intravenous Trappsol Cyclo (HPβCD) in Niemann-Pick Diseas
NCT03893071
Cyclo Therapeutics, Inc.Phase 1
Enrolling By InvitationEarly Check: Expanded Screening in Newborns
NCT03655223
RTI International—
CompletedStudy of the Pharmacokinetics of Trappsol and Effects on Potential Biomarkers of Niemann-Pick C1 (NPC1)
NCT02939547
Cyclo Therapeutics, Inc.Phase 1
UnknownStudy of Lithium Carbonate to Treat Niemann-Pick Type C1 Disease
NCT03201627
Xinhua Hospital, Shanghai Jiao Tong University School of MedicineEARLY_Phase 1
CompletedSafety and Efficacy of Intravenous Trappsol Cyclo (HPBCD) in Niemann-Pick Type C Patients
NCT02912793
Cyclo Therapeutics, Inc.Phase 1 / Phase 2
CompletedHydroxypropyl Beta Cyclodextrin for Niemann-Pick Type C1 Disease
NCT01747135
Vtesse, LLC, a Mallinckrodt Pharmaceuticals CompanyPhase 1