Clinical Trials Directory

Trials / Conditions / NGLY1 Deficiency

NGLY1 Deficiency

3 registered clinical trials studyying NGLY1 Deficiency1 currently recruiting.

StatusTrialSponsorPhase
Active Not RecruitingA Study of GlcNAc on Tear Production in NGLY1-CDDG
NCT05402345
Eva Morava-KoziczPhase 2
RecruitingSafety and Efficacy of GS-100 Gene Therapy in Patients With NGLY1 Deficiency
NCT06199531
Grace Science, LLCPhase 1 / Phase 2
CompletedNGLY1 Natural History
NCT06122766
Baylor College of Medicine