Trials / Conditions / Neurogenetic Disorders
Neurogenetic Disorders
3 registered clinical trials studyying Neurogenetic Disorders — 3 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Not Yet Recruiting | Safety and Efficacy of AAV9/AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type NCT06948019 | BlackfinBio Ltd | Phase 1 / Phase 2 |
| Recruiting | Pediatric Neurogenetic Diagnosis Support Platform NCT06725901 | Universidad Nacional Andres Bello | N/A |
| Recruiting | Neurogenetics Patient Registry NCT02995538 | University of Pittsburgh | — |