Clinical Trials Directory

Trials / Conditions / Myotonic Disorders

Myotonic Disorders

7 registered clinical trials studyying Myotonic Disorders2 currently recruiting.

StatusTrialSponsorPhase
RecruitingProspective, Long Term, Observational Study (Patient Registry) of Paediatric Myotonic Disorders
NCT07154654
Lupin Ltd.
Enrolling By InvitationGlobal Open-Label Extension Study of Del-desiran for the Treatment of DM1
NCT07008469
Avidity Biosciences, Inc.Phase 3
Active Not RecruitingGlobal Study of Del-desiran for the Treatment of DM1
NCT06411288
Avidity Biosciences, Inc.Phase 3
CompletedExtension of AOC 1001-CS1 (MARINA) Study in Adult Myotonic Dystrophy Type 1 (DM1) Patients
NCT05479981
Avidity Biosciences, Inc.Phase 2
Active Not RecruitingOpen-label Extension Study in Paediatric Patients Who Have Completed the MEX-NM-301 Study.
NCT04622553
Lupin Ltd.N/A
CompletedStudy of AOC 1001 in Adult Myotonic Dystrophy Type 1 (DM1) Patients
NCT05027269
Avidity Biosciences, Inc.Phase 1 / Phase 2
CompletedCharacteristics of Nondystrophic Myotonias
NCT00244413
Richard Barohn, MD