Trials / Conditions / Mucopolysaccharidosis Type 7
Mucopolysaccharidosis Type 7
3 registered clinical trials studyying Mucopolysaccharidosis Type 7 — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Enrolling By Invitation | Early Check: Expanded Screening in Newborns NCT03655223 | RTI International | — |
| Completed | An Open-Label Phase 1/2 Study to Assess the Safety, Efficacy and Dose of Study Drug UX003 Recombinant Human Be NCT01856218 | Ultragenyx Pharmaceutical Inc | Phase 1 / Phase 2 |
| No Longer Available | An Open-Label Treatment Protocol With UX003 rhGUS Enzyme Replacement Therapy for an Advanced Stage MPS 7 Patie NCT02097251 | Joyce Fox | — |