Trials / Conditions / Mucopolysaccharidosis IVA
Mucopolysaccharidosis IVA
6 registered clinical trials studyying Mucopolysaccharidosis IVA.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Terminated | Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation NCT01697319 | BioMarin Pharmaceutical | Phase 2 |
| Terminated | Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome NCT01609062 | BioMarin Pharmaceutical | Phase 2 |
| Completed | Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome) NCT01515956 | BioMarin Pharmaceutical | Phase 2 |
| Terminated | A Study to Evaluate the Long-Term Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (M NCT01242111 | BioMarin Pharmaceutical | Phase 1 / Phase 2 |
| Terminated | A Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome) NCT00787995 | BioMarin Pharmaceutical | — |
| Approved For Marketing | BMN 110 US Expanded Access Program NCT01858103 | BioMarin Pharmaceutical | — |