Trials / Conditions / Mucopolysaccharidosis IV A

Mucopolysaccharidosis IV A

8 registered clinical trials studyying Mucopolysaccharidosis IV A — 2 currently recruiting.

Status	Trial	Sponsor	Phase
Completed	Baby Detect : Genomic Newborn Screening NCT05687474	Centre Hospitalier Universitaire de Liege	—
Recruiting	Registry of Patients Diagnosed With Lysosomal Storage Diseases NCT05619900	University of California, San Francisco	—
Enrolling By Invitation	ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program NCT05368038	Albert Einstein College of Medicine	—
Unknown	Evaluation of Losartan on Cardiovascular Disease in Patients With Mucopolysaccharidoses IV A and VI NCT03632213	Hospital de Clinicas de Porto Alegre	Phase 2
Completed	Natural History of Atypical Morquio A Disease NCT03204370	GOIZET	—
Completed	Psychological Concomitants of Morquio A Syndrome - Longitudinal Effects of Enzyme Replacement Therapy (The MAP NCT02208661	Nadia Ali, PhD	—
Completed	Diagnosis of Mucopolysaccharidosis Disorders in Patients Presenting With Bilateral Hip Disease NCT01707433	Children's Hospitals and Clinics of Minnesota	—
Completed	Long-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A NCT01415427	BioMarin Pharmaceutical	Phase 3