Clinical Trials Directory

Trials / Conditions / MPS IV A

MPS IV A

6 registered clinical trials studyying MPS IV A1 currently recruiting.

StatusTrialSponsorPhase
RecruitingCardiac Structure and Function in MPS
NCT07361536
Children's Hospital of Orange County
UnknownEvaluation of Losartan on Cardiovascular Disease in Patients With Mucopolysaccharidoses IV A and VI
NCT03632213
Hospital de Clinicas de Porto AlegrePhase 2
CompletedA Double-Blind Study to Evaluate the Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA
NCT01275066
BioMarin PharmaceuticalPhase 3
TerminatedA Study to Evaluate the Long-Term Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (M
NCT01242111
BioMarin PharmaceuticalPhase 1 / Phase 2
CompletedA Study to Evaluate the Safety, Tolerability and Efficacy of BMN 110 in Subjects With Mucopolysaccharidosis IV
NCT00884949
BioMarin PharmaceuticalPhase 1 / Phase 2
TerminatedA Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)
NCT00787995
BioMarin Pharmaceutical