MPS I

8 registered clinical trials studyying MPS I — 3 currently recruiting.

Status	Trial	Sponsor	Phase
Recruiting	Cardiac Structure and Function in MPS NCT07361536	Children's Hospital of Orange County	—
Withdrawn	Safety and Efficacy of Encapsulated Allogeneic MPS-1 Therapy NCT05665036	Sigilon Therapeutics, Inc.	Phase 1 / Phase 2
Unknown	The Intensively Follow-up Examinations for Asymptomatic MPS I Infants in Taiwan NCT04958070	Mackay Memorial Hospital	—
Recruiting	PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders) NCT04532047	University of California, San Francisco	Phase 1
Terminated	Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-318 in Subjects With M NCT02702115	Sangamo Therapeutics	Phase 1 / Phase 2
Completed	Ultrasound Findings of Finger, Wrist and Knee Joints in Mucopolysaccharidosis NCT02067650	Children's Hospital of Eastern Ontario	—
Terminated	Laronidase (Aldurazyme TM) Enzyme Replacement Therapy With Hematopoietic Stem Cell Transplant for Hurler Syndr NCT01572636	Masonic Cancer Center, University of Minnesota	—
Recruiting	Longitudinal Study of Neurodegenerative Disorders NCT03333200	University of Pittsburgh	—