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Trials / Conditions / Morquio A Syndrome

Morquio A Syndrome

11 registered clinical trials studyying Morquio A Syndrome1 currently recruiting.

StatusTrialSponsorPhase
RecruitingNon-invasive Functional Assessment and Pathogenesis of Morquio A
NCT05284006
Nemours Children's Clinic
UnknownEvaluation of Losartan on Cardiovascular Disease in Patients With Mucopolysaccharidoses IV A and VI
NCT03632213
Hospital de Clinicas de Porto AlegrePhase 2
CompletedA Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
NCT02294877
BioMarin Pharmaceutical
CompletedPsychological Concomitants of Morquio A Syndrome - Longitudinal Effects of Enzyme Replacement Therapy (The MAP
NCT02208661
Nadia Ali, PhD
TerminatedEfficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation
NCT01697319
BioMarin PharmaceuticalPhase 2
TerminatedSafety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome
NCT01609062
BioMarin PharmaceuticalPhase 2
CompletedStudy of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome)
NCT01515956
BioMarin PharmaceuticalPhase 2
CompletedLong-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A
NCT01415427
BioMarin PharmaceuticalPhase 3
TerminatedA Study to Evaluate the Long-Term Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (M
NCT01242111
BioMarin PharmaceuticalPhase 1 / Phase 2
TerminatedA Clinical Assessment Study of Subjects With Mucopolysaccharidosis IVA (Morquio Syndrome)
NCT00787995
BioMarin Pharmaceutical
Approved For MarketingBMN 110 US Expanded Access Program
NCT01858103
BioMarin Pharmaceutical