Clinical Trials Directory

Trials / Conditions / Mitochondrial Trifunctional Protein Deficiency

Mitochondrial Trifunctional Protein Deficiency

3 registered clinical trials studyying Mitochondrial Trifunctional Protein Deficiency1 currently recruiting.

StatusTrialSponsorPhase
Enrolling By InvitationEarly Check: Expanded Screening in Newborns
NCT03655223
RTI International
TerminatedVitamin E Treatment for Long-Chain 3-Hydroxyacyl Coenzyme A (CoA) Dehydrogenase (LCHAD) Associated Neuropathy
NCT00840112
Oregon Health and Science UniversityN/A
No Longer AvailableCompassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism
NCT01461304
Jerry Vockley, MD, PhD