Trials / Conditions / Leber Congenital Amaurosis 10
Leber Congenital Amaurosis 10
6 registered clinical trials studyying Leber Congenital Amaurosis 10 — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION) NCT06891443 | Laboratoires Thea | Phase 3 |
| Unknown | An Open-label, Dose Escalation and Double-masked, Randomized, Controlled Trial Evaluating Safety and Tolerabil NCT04855045 | ProQR Therapeutics | Phase 2 / Phase 3 |
| Unknown | Single Ascending Dose Study in Participants With LCA10 NCT03872479 | Editas Medicine, Inc. | Phase 1 / Phase 2 |
| Terminated | Extension Study to Study PQ-110-001 (NCT03140969) NCT03913130 | Laboratoires Thea | Phase 1 / Phase 2 |
| Active Not Recruiting | A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in NCT03913143 | ProQR Therapeutics | Phase 2 / Phase 3 |
| Completed | Natural History Study of CEP290-Related Retinal Degeneration NCT03396042 | Editas Medicine, Inc. | — |