Trials / Conditions / Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2
Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2
4 registered clinical trials studyying Late-Infantile Neuronal Ceroid Lipofuscinosis Type 2.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Active Not Recruiting | Cerliponase Alfa Observational Study in the US NCT04476862 | BioMarin Pharmaceutical | — |
| Completed | A Safety, Tolerability, and Efficacy Study of BMN 190 in Pediatric Patients < 18 Years of Age With CLN2 Diseas NCT02678689 | BioMarin Pharmaceutical | Phase 2 |
| Completed | An Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease NCT02485899 | BioMarin Pharmaceutical | Phase 1 / Phase 2 |
| Completed | A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Efficacy NCT01907087 | BioMarin Pharmaceutical | Phase 1 / Phase 2 |