Krabbe Disease

13 registered clinical trials studyying Krabbe Disease — 4 currently recruiting.

Status	Trial	Sponsor	Phase
Terminated	Long-term Follow-up Study to Evaluate Safety and Efficacy of FBX-101 in Krabbe Patients NCT06308718	Forge Biologics, Inc	—
Active Not Recruiting	Gene Transfer Clinical Trial for Infantile and Late Infantile Krabbe Disease Treated Previously With HSCT NCT05739643	Forge Biologics, Inc	Phase 1 / Phase 2
Active Not Recruiting	Gene Transfer Clinical Trial for Krabbe Disease NCT04693598	Forge Biologics, Inc	Phase 1 / Phase 2
Enrolling By Invitation	Early Check: Expanded Screening in Newborns NCT03655223	RTI International	—
Withdrawn	Biomarker for Krabbe Disease (BioKrabbe) NCT01425489	CENTOGENE GmbH Rostock	—
Completed	LeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies NCT02699190	Children's Hospital of Philadelphia	—
Recruiting	The Myelin Disorders Biorepository Project NCT03047369	Children's Hospital of Philadelphia	—
Recruiting	Krabbe Disease Global Patient Registry NCT02993796	State University of New York at Buffalo	—
Recruiting	Longitudinal Study of Neurodegenerative Disorders NCT03333200	University of Pittsburgh	—
Completed	Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders NCT01043640	Masonic Cancer Center, University of Minnesota	Phase 2
Completed	Lysosomal Storage Disease: Health, Development, and Functional Outcome Surveillance in Preschool Children NCT01938014	University of Chicago	—
Active Not Recruiting	Diffusion Tensor Imaging (DTI) in Infants With Krabbe Disease NCT00787865	University of Pittsburgh	—
Terminated	Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism NCT00668564	Masonic Cancer Center, University of Minnesota	Phase 2